2024 Journal Article Neutrophil-to-lymphocyte ratio at diagnosis as a biomarker for survival of amyotrophic lateral sclerosisNona, Robert J., Henderson, Robert D. and McCombe, Pamela A. (2024). Neutrophil-to-lymphocyte ratio at diagnosis as a biomarker for survival of amyotrophic lateral sclerosis. Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration, 25 (5-6), 452-464. doi: 10.1080/21678421.2024.2351187 |
2024 Journal Article Routine CSF parameters as predictors of disease course in multiple sclerosis: an MSBase cohort studyDekeyser, Cathérine, Hautekeete, Matthias, Cambron, Melissa, Van Pesch, Vincent, Patti, Francesco, Kuhle, Jens, Khoury, Samia, Lechner Scott, Jeanette, Gerlach, Oliver, Lugaresi, Alessandra, Maimone, Davide, Surcinelli, Andrea, Grammond, Pierre, Kalincik, Tomas, Habek, Mario, Willekens, Barbara, Macdonell, Richard, Lalive, Patrice, Csepany, Tunde, Butzkueven, Helmut, Boz, Cavit, Tomassini, Valentina, Foschi, Matteo, Sánchez-Menoyo, José Luis, Altintas, Ayse, Mrabet, Saloua, Iuliano, Gerardo, Sa, Maria Jose, Alroughani, Raed ... Laureys, Guy (2024). Routine CSF parameters as predictors of disease course in multiple sclerosis: an MSBase cohort study. Journal of Neurology, Neurosurgery and Psychiatry, 95 (11), 1021-1031. doi: 10.1136/jnnp-2023-333307 |
2024 Journal Article Vitamin D did not reduce multiple sclerosis disease activity after a clinically isolated syndromeButzkueven, Helmut, Ponsonby, Anne-Louise, Stein, Mark S., Lucas, Robyn M., Mason, Deborah, Broadley, Simon, Kilpatrick, Trevor, Lechner-Scott, Jeannette, Barnett, Michael, Carroll, William, Mitchell, Peter, Hardy, Todd A., Macdonell, Richard, Mccombe, Pamela, Lee, Andrew, Kalincik, Tomas, van der Walt, Anneke, Lynch, Chris, Abernethy, David, Willoughby, Ernest, Barkhof, Frederik, Macmanus, David, Clarke, Michael, Andrew, Julie, Morahan, Julia, Zhu, Chao, Dear, Keith and Taylor, Bruce (2024). Vitamin D did not reduce multiple sclerosis disease activity after a clinically isolated syndrome. Brain, 147 (4), 1206-1215. doi: 10.1093/brain/awad409 |
2024 Journal Article Long-term efficacy and safety of Rituximab in the treatment of neuromyelitis optica spectrum disorderHayes, Michael Thomas Gerard, Adam, Robert J., McCombe, Pamela Ann, Walsh, Michael and Blum, Stefan (2024). Long-term efficacy and safety of Rituximab in the treatment of neuromyelitis optica spectrum disorder. Multiple Sclerosis Journal, 10 (2) 20552173241257876, 20552173241257876. doi: 10.1177/20552173241257876 |
2024 Journal Article Transient binocular vision loss and pain insensitivity in Klippel–Feil syndrome: a case reportUllah, Zeeshan, Zafar, Ayesha, Ishaq, Hira, Umar, Zainab, Khan, Amir, Badar, Yaseen, Din, Nizamud, Khan, Muhammad Fawad, McCombe, Pamela and Khan, Nemat (2024). Transient binocular vision loss and pain insensitivity in Klippel–Feil syndrome: a case report. Journal of Medical Case Reports, 18 (1) 137, 1-6. doi: 10.1186/s13256-024-04374-w |
2024 Journal Article Variation in resting metabolic rate affects identification of metabolic change in geographically distinct cohorts of patients with ALSHoldom, Cory J., Janse van Mantgem, Mark R., He, Ji, Howe, Stephanie L., McCombe, Pamela A., Fan, Dongsheng, van den Berg, Leonard H., Henderson, Robert D., van Eijk, Ruben, Steyn, Frederik J. and Ngo, Shyuan T. (2024). Variation in resting metabolic rate affects identification of metabolic change in geographically distinct cohorts of patients with ALS. Neurology, 102 (5) e208117, 1-11. doi: 10.1212/wnl.0000000000208117 |
2024 Journal Article Gut symptoms, gut dysbiosis and gut-derived toxins in ALSLee, Aven, Henderson, Robert, Aylward, James and McCombe, Pamela (2024). Gut symptoms, gut dysbiosis and gut-derived toxins in ALS. International Journal of Molecular Sciences, 25 (3) 1871, 1-25. doi: 10.3390/ijms25031871 |
2024 Journal Article Examining the environmental risk factors of progressive-onset and relapsing-onset multiple sclerosis: recruitment challenges, potential bias, and statistical strategiesLi, Ying, Saul, Alice, Taylor, Bruce, Ponsonby, Anne-Louise, Simpson-Yap, Steve, Blizzard, Leigh, Broadley, Simon, Lechner-Scott, Jeannette, Lucas, Robyn, Dear, Keith, Ponsonby, Anne-Louise, Dwyer, Terry, van der Mei, Ingrid, Blizzard, Leigh, Simpson-Yap, Steve, Taylor, Bruce, Broadley, Simon, Kilpatrick, Trevor, Williams, David, Lechner-Scott, Jeanette, Shaw, Cameron, Chapman, Caron, Coulthard, Alan, Pender, Michael, Valery, Patricia, Karabudak, Rana, Patti, Francesco, Eichau, Sara, Onofrj, Marco ... van der Mei, Ingrid (2024). Examining the environmental risk factors of progressive-onset and relapsing-onset multiple sclerosis: recruitment challenges, potential bias, and statistical strategies. Journal of Neurology, 271 (1), 472-485. doi: 10.1007/s00415-023-11980-z |
2024 Journal Article Comparative effectiveness and cost-effectiveness of natalizumab and fingolimod in rapidly evolving severe relapsing-remitting multiple sclerosis in the United KingdomSpelman, T., Herring, W. L., Acosta, C., Hyde, R., Jokubaitis, V. G., Pucci, E., Lugaresi, A., Laureys, G., Havrdova, E. K., Horakova, D., Izquierdo, G., Eichau, S., Ozakbas, S., Alroughani, R., Kalincik, T., Duquette, P., Girard, M., Petersen, T., Patti, F., Csepany, T., Granella, F., Grand’Maison, F., Ferraro, D., Karabudak, R., Jose Sa, M., Trojano, M., van Pesch, V., Van Wijmeersch, B., Cartechini, E. ... Butzkueven, H. (2024). Comparative effectiveness and cost-effectiveness of natalizumab and fingolimod in rapidly evolving severe relapsing-remitting multiple sclerosis in the United Kingdom. Journal of Medical Economics, 27 (1), 109-125. doi: 10.1080/13696998.2023.2293379 |
2024 Journal Article Comparative efficacy of ofatumumab versus oral therapies for relapsing multiple sclerosis patients using propensity score analyses and simulated treatment comparisonsRiley, Nicholas, Drudge, Christopher, Nelson, Morag, Haltner, Anja, Barnett, Michael, Broadley, Simon, Butzkueven, Helmut, McCombe, Pamela, Van der Walt, Anneke, Wong, Erin O. Y., Merschhemke, Martin, Adlard, Nicholas, Walker, Rob and Samjoo, Imtiaz A. (2024). Comparative efficacy of ofatumumab versus oral therapies for relapsing multiple sclerosis patients using propensity score analyses and simulated treatment comparisons. Therapeutic Advances in Neurological Disorders, 17 17562864241239453. doi: 10.1177/17562864241239453 |
2024 Journal Article Associations of postprandial ghrelin, liver‐expressed antimicrobial peptide 2 and leptin levels with body composition, disease progression and survival in patients with amyotrophic lateral sclerosisHowe, Stephanie L., Holdom, Cory J., McCombe, Pamela A., Henderson, Robert D., Zigman, Jeffrey M., Ngo, Shyuan T. and Steyn, Frederik J. (2024). Associations of postprandial ghrelin, liver‐expressed antimicrobial peptide 2 and leptin levels with body composition, disease progression and survival in patients with amyotrophic lateral sclerosis. European Journal of Neurology, 31 (1) e16052, e16052. doi: 10.1111/ene.16052 |
2024 Journal Article Onboarding of siponimod in secondary progressive multiple sclerosis patients in Australia: Novel, real-world evidence from the MSGo digital support programmeHardy, TA, Aouad, P, Barnett, MH, Blum, S, Broadley, S, Carroll, WM, Crimmins, D, Griffiths, D, Hodgkinson, S, Lechner-Scott, J, Lee, A, Malhotra, R, McCombe, P, Parratt, J, Plummer, C, Van der Walt, A, Martel, K and Walker, RA (2024). Onboarding of siponimod in secondary progressive multiple sclerosis patients in Australia: Novel, real-world evidence from the MSGo digital support programme. Multiple Sclerosis Journal - Experimental, Translational and Clinical, 10 (1) 20552173231226106, 20552173231226106. doi: 10.1177/20552173231226106 |
2023 Journal Article Predictors of treatment switching in the Big Multiple Sclerosis Data NetworkSpelman, Tim, Magyari, Melinda, Butzkueven, Helmut, Van Der Walt, Anneke, Vukusic, Sandra, Trojano, Maria, Iaffaldano, Pietro, Horáková, Dana, Drahota, Jirí, Pellegrini, Fabio, Hyde, Robert, Duquette, Pierre, Lechner-Scott, Jeannette, Sajedi, Seyed Aidin, Lalive, Patrice, Shaygannejad, Vahid, Ozakbas, Serkan, Eichau, Sara, Alroughani, Raed, Terzi, Murat, Girard, Marc, Kalincik, Tomas, Grand'Maison, Francois, Skibina, Olga, Khoury, Samia J., Yamout, Bassem, Sa, Maria Jose, Gerlach, Oliver, Blanco, Yolanda ... Hillert, Jan (2023). Predictors of treatment switching in the Big Multiple Sclerosis Data Network. Frontiers in Neurology, 14 1274194, 1-10. doi: 10.3389/fneur.2023.1274194 |
2023 Journal Article Longitudinal changes in intrinsic motoneuron excitability in amyotrophic lateral sclerosis are dependent on disease progressionTrajano, Gabriel S., Orssatto, Lucas B. R., McCombe, Pamela A., Rivlin, Warwick, Tang, Lily and Henderson, Robert D. (2023). Longitudinal changes in intrinsic motoneuron excitability in amyotrophic lateral sclerosis are dependent on disease progression. The Journal of Physiology, 601 (21), 4723-4735. doi: 10.1113/jp285181 |
2023 Journal Article The risk of secondary progressive multiple sclerosis is geographically determined but modifiableSharmin, Sifat, Roos, Izanne, Simpson-Yap, Steve, Malpas, Charles, Sánchez, Marina M, Ozakbas, Serkan, Horakova, Dana, Havrdova, Eva K., Patti, Francesco, Alroughani, Raed, Izquierdo, Guillermo, Eichau, Sara, Boz, Cavit, Zakaria, Magd, Onofrj, Marco, Lugaresi, Alessandra, Weinstock-Guttman, Bianca, Prat, Alexandre, Girard, Marc, Duquette, Pierre, Terzi, Murat, Amato, Maria Pia, Karabudak, Rana, Grand'Maison, Francois, Khoury, Samia J., Grammond, Pierre, Lechner-Scott, Jeannette, Buzzard, Katherine, Skibina, Olga ... Kalincik, Tomas (2023). The risk of secondary progressive multiple sclerosis is geographically determined but modifiable. Brain, 146 (11), 4633-4644. doi: 10.1093/brain/awad218 |
2023 Journal Article Examining the environmental risk factors of progressive-onset and relapsing-onset multiple sclerosis: recruitment challenges, potential bias, and statistical strategiesLi, Ying, Saul, Alice, Taylor, Bruce, Ponsonby, Anne-Louise, Simpson-Yap, Steve, Blizzard, Leigh, Broadley, Simon, Lechner-Scott, Jeannette, Lucas, Robyn, Dear, Keith, Ponsonby, Anne-Louise, Dwyer, Terry, van der Mei, Ingrid, Blizzard, Leigh, Simpson-Yap, Steve, Taylor, Bruce, Broadley, Simon, Kilpatrick, Trevor, Williams, David, Lechner-Scott, Jeanette, Shaw, Cameron, Chapman, Caron, Coulthard, Alan, Pender, Michael (AusImmune/AusLong Investigators Group member), Valery, Patricia, Karabudak, Rana, Patti, Francesco, Eichau, Sara, Onofrj, Marco ... MSBase (2023). Examining the environmental risk factors of progressive-onset and relapsing-onset multiple sclerosis: recruitment challenges, potential bias, and statistical strategies. Journal of Neurology, 271 (1), 1-14. doi: 10.1007/s00415-023-11980-z |
2023 Journal Article Proteomic investigation of ALS motor cortex identifies known and novel pathogenetic mechanismsLee, Aven, Henderson, Robert, Jayakody Arachchige, Buddhika, Robertson, Thomas and McCombe, Pamela Ann (2023). Proteomic investigation of ALS motor cortex identifies known and novel pathogenetic mechanisms. Journal of the Neurological Sciences, 452 120753, 120753. doi: 10.1016/j.jns.2023.120753 |
2023 Journal Article Disability accrual in primary and secondary progressive multiple sclerosisHarding-Forrester, Sam, Roos, Izanne, Nguyen, Ai-Lan, Malpas, Charles B., Diouf, Ibrahima, Moradi, Nahid, Sharmin, Sifat, Izquierdo, Guillermo, Eichau, Sara, Patti, Francesco, Horakova, Dana, Kubala Havrdova, Eva, Prat, Alexandre, Girard, Marc, Duquette, Pierre, Grand'Maison, Francois, Onofrj, Marco, Lugaresi, Alessandra, Grammond, Pierre, Ozakbas,, Serkan, Amato, Maria Pia, Gerlach, Oliver, Sola, Patrizia, Ferraro, Diana, Buzzard, Katherine, Skibina, Olga, Lechner-Scott, Jeannette, Alroughani, Raed, Boz, Cavit ... Kalincik, Tomas (2023). Disability accrual in primary and secondary progressive multiple sclerosis. Journal of Neurology, Neurosurgery and Psychiatry, 94 (9) 330726, 1-11. doi: 10.1136/jnnp-2022-330726 |
2023 Journal Article Effectiveness of multiple disease-modifying therapies in relapsing-remitting multiple sclerosis: causal inference to emulate a multiarm randomised trialDiouf, Ibrahima, Malpas, Charles B, Sharmin, Sifat, Roos, Izanne, Horakova, Dana, Kubala Havrdova, Eva, Patti, Francesco, Shaygannejad, Vahid, Ozakbas, Serkan, Eichau, Sara, Onofrj, Marco, Lugaresi, Alessandra, Alroughani, Raed, Prat, Alexandre, Duquette, Pierre, Terzi, Murat, Boz, Cavit, Grand'Maison, Francois, Sola, Patrizia, Ferraro, Diana, Grammond, Pierre, Yamout, Bassem, Altintas, Ayse, Gerlach, Oliver, Lechner-Scott, Jeannette, Bergamaschi, Roberto, Karabudak, Rana, Iuliano, Gerardo, McGuigan, Christopher ... Kalincik, Tomas (2023). Effectiveness of multiple disease-modifying therapies in relapsing-remitting multiple sclerosis: causal inference to emulate a multiarm randomised trial. Journal of Neurology, Neurosurgery and Psychiatry, 94 (12), jnnp-2023. doi: 10.1136/jnnp-2023-331499 |
2023 Journal Article Early non-disabling relapses are important predictors of disability accumulation in people with relapsing-remitting multiple sclerosisDaruwalla, Cyrus, Shaygannejad, Vahid, Ozakbas, Serkan, Havrdova, Eva Kubala, Horakova, Dana, Alroughani, Raed, Boz, Cavit, Patti, Francesco, Onofrj, Marco, Lugaresi, Alessandra, Eichau, Sara, Girard, Marc, Prat, Alexandre, Duquette, Pierre, Yamout, Bassem, Khoury, Samia J., Sajedi, Seyed Aidin, Turkoglu, Recai, Altintas, Ayse, Skibina, Olga, Buzzard, Katherine, Grammond, Pierre, Karabudak, Rana, van der Walt, Anneke, Butzkueven, Helmut, Maimone, Davide, Lechner-Scott, Jeannette, Soysal, Aysun, John, Nevin ... Brown, J William L (2023). Early non-disabling relapses are important predictors of disability accumulation in people with relapsing-remitting multiple sclerosis. Multiple Sclerosis, 29 (7), 875-883. doi: 10.1177/13524585231151951 |