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2024 Journal Article Comparative efficacy of ofatumumab versus oral therapies for relapsing multiple sclerosis patients using propensity score analyses and simulated treatment comparisonsRiley, Nicholas, Drudge, Christopher, Nelson, Morag, Haltner, Anja, Barnett, Michael, Broadley, Simon, Butzkueven, Helmut, McCombe, Pamela, Van der Walt, Anneke, Wong, Erin O. Y., Merschhemke, Martin, Adlard, Nicholas, Walker, Rob and Samjoo, Imtiaz A. (2024). Comparative efficacy of ofatumumab versus oral therapies for relapsing multiple sclerosis patients using propensity score analyses and simulated treatment comparisons. Therapeutic Advances in Neurological Disorders, 17 17562864241239453. doi: 10.1177/17562864241239453 |
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2024 Journal Article Comparative effectiveness and cost-effectiveness of natalizumab and fingolimod in rapidly evolving severe relapsing-remitting multiple sclerosis in the United KingdomSpelman, T., Herring, W. L., Acosta, C., Hyde, R., Jokubaitis, V. G., Pucci, E., Lugaresi, A., Laureys, G., Havrdova, E. K., Horakova, D., Izquierdo, G., Eichau, S., Ozakbas, S., Alroughani, R., Kalincik, T., Duquette, P., Girard, M., Petersen, T., Patti, F., Csepany, T., Granella, F., Grand’Maison, F., Ferraro, D., Karabudak, R., Jose Sa, M., Trojano, M., van Pesch, V., Van Wijmeersch, B., Cartechini, E. ... Butzkueven, H. (2024). Comparative effectiveness and cost-effectiveness of natalizumab and fingolimod in rapidly evolving severe relapsing-remitting multiple sclerosis in the United Kingdom. Journal of Medical Economics, 27 (1), 109-125. doi: 10.1080/13696998.2023.2293379 |
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2023 Journal Article Predictors of treatment switching in the Big Multiple Sclerosis Data NetworkSpelman, Tim, Magyari, Melinda, Butzkueven, Helmut, Van Der Walt, Anneke, Vukusic, Sandra, Trojano, Maria, Iaffaldano, Pietro, Horáková, Dana, Drahota, Jirí, Pellegrini, Fabio, Hyde, Robert, Duquette, Pierre, Lechner-Scott, Jeannette, Sajedi, Seyed Aidin, Lalive, Patrice, Shaygannejad, Vahid, Ozakbas, Serkan, Eichau, Sara, Alroughani, Raed, Terzi, Murat, Girard, Marc, Kalincik, Tomas, Grand'Maison, Francois, Skibina, Olga, Khoury, Samia J., Yamout, Bassem, Sa, Maria Jose, Gerlach, Oliver, Blanco, Yolanda ... Hillert, Jan (2023). Predictors of treatment switching in the Big Multiple Sclerosis Data Network. Frontiers in Neurology, 14 1274194, 1-10. doi: 10.3389/fneur.2023.1274194 |
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2023 Journal Article Longitudinal changes in intrinsic motoneuron excitability in amyotrophic lateral sclerosis are dependent on disease progressionTrajano, Gabriel S., Orssatto, Lucas B. R., McCombe, Pamela A., Rivlin, Warwick, Tang, Lily and Henderson, Robert D. (2023). Longitudinal changes in intrinsic motoneuron excitability in amyotrophic lateral sclerosis are dependent on disease progression. The Journal of Physiology, 601 (21), 4723-4735. doi: 10.1113/jp285181 |
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2023 Journal Article The risk of secondary progressive multiple sclerosis is geographically determined but modifiableSharmin, Sifat, Roos, Izanne, Simpson-Yap, Steve, Malpas, Charles, Sánchez, Marina M, Ozakbas, Serkan, Horakova, Dana, Havrdova, Eva K., Patti, Francesco, Alroughani, Raed, Izquierdo, Guillermo, Eichau, Sara, Boz, Cavit, Zakaria, Magd, Onofrj, Marco, Lugaresi, Alessandra, Weinstock-Guttman, Bianca, Prat, Alexandre, Girard, Marc, Duquette, Pierre, Terzi, Murat, Amato, Maria Pia, Karabudak, Rana, Grand'Maison, Francois, Khoury, Samia J., Grammond, Pierre, Lechner-Scott, Jeannette, Buzzard, Katherine, Skibina, Olga ... Kalincik, Tomas (2023). The risk of secondary progressive multiple sclerosis is geographically determined but modifiable. Brain, 146 (11), 4633-4644. doi: 10.1093/brain/awad218 |
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2023 Journal Article Examining the environmental risk factors of progressive-onset and relapsing-onset multiple sclerosis: recruitment challenges, potential bias, and statistical strategiesLi, Ying, Saul, Alice, Taylor, Bruce, Ponsonby, Anne-Louise, Simpson-Yap, Steve, Blizzard, Leigh, Broadley, Simon, Lechner-Scott, Jeannette, Lucas, Robyn, Dear, Keith, Ponsonby, Anne-Louise, Dwyer, Terry, van der Mei, Ingrid, Blizzard, Leigh, Simpson-Yap, Steve, Taylor, Bruce, Broadley, Simon, Kilpatrick, Trevor, Williams, David, Lechner-Scott, Jeanette, Shaw, Cameron, Chapman, Caron, Coulthard, Alan, Pender, Michael (AusImmune/AusLong Investigators Group member), Valery, Patricia, Karabudak, Rana, Patti, Francesco, Eichau, Sara, Onofrj, Marco ... MSBase (2023). Examining the environmental risk factors of progressive-onset and relapsing-onset multiple sclerosis: recruitment challenges, potential bias, and statistical strategies. Journal of Neurology, 271 (1), 1-14. doi: 10.1007/s00415-023-11980-z |
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2023 Journal Article Proteomic investigation of ALS motor cortex identifies known and novel pathogenetic mechanismsLee, Aven, Henderson, Robert, Jayakody Arachchige, Buddhika, Robertson, Thomas and McCombe, Pamela Ann (2023). Proteomic investigation of ALS motor cortex identifies known and novel pathogenetic mechanisms. Journal of the Neurological Sciences, 452 120753, 120753. doi: 10.1016/j.jns.2023.120753 |
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2023 Journal Article Disability accrual in primary and secondary progressive multiple sclerosisHarding-Forrester, Sam, Roos, Izanne, Nguyen, Ai-Lan, Malpas, Charles B., Diouf, Ibrahima, Moradi, Nahid, Sharmin, Sifat, Izquierdo, Guillermo, Eichau, Sara, Patti, Francesco, Horakova, Dana, Kubala Havrdova, Eva, Prat, Alexandre, Girard, Marc, Duquette, Pierre, Grand'Maison, Francois, Onofrj, Marco, Lugaresi, Alessandra, Grammond, Pierre, Ozakbas,, Serkan, Amato, Maria Pia, Gerlach, Oliver, Sola, Patrizia, Ferraro, Diana, Buzzard, Katherine, Skibina, Olga, Lechner-Scott, Jeannette, Alroughani, Raed, Boz, Cavit ... Kalincik, Tomas (2023). Disability accrual in primary and secondary progressive multiple sclerosis. Journal of Neurology, Neurosurgery and Psychiatry, 94 (9) 330726, 1-11. doi: 10.1136/jnnp-2022-330726 |
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2023 Journal Article Effectiveness of multiple disease-modifying therapies in relapsing-remitting multiple sclerosis: causal inference to emulate a multiarm randomised trialDiouf, Ibrahima, Malpas, Charles B, Sharmin, Sifat, Roos, Izanne, Horakova, Dana, Kubala Havrdova, Eva, Patti, Francesco, Shaygannejad, Vahid, Ozakbas, Serkan, Eichau, Sara, Onofrj, Marco, Lugaresi, Alessandra, Alroughani, Raed, Prat, Alexandre, Duquette, Pierre, Terzi, Murat, Boz, Cavit, Grand'Maison, Francois, Sola, Patrizia, Ferraro, Diana, Grammond, Pierre, Yamout, Bassem, Altintas, Ayse, Gerlach, Oliver, Lechner-Scott, Jeannette, Bergamaschi, Roberto, Karabudak, Rana, Iuliano, Gerardo, McGuigan, Christopher ... Kalincik, Tomas (2023). Effectiveness of multiple disease-modifying therapies in relapsing-remitting multiple sclerosis: causal inference to emulate a multiarm randomised trial. Journal of Neurology, Neurosurgery and Psychiatry, 94 (12), jnnp-2023. doi: 10.1136/jnnp-2023-331499 |
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2023 Conference Publication Novel real world evidence from MSGo, a digital support program for secondary progressive multiple sclerosis patients in Australia using SiponimodHardy, Todd, Aouad, Patrick, Barnett, Michael, Blum, Stefan, Broadley, Simon, Carroll, William, Crimmins, Denis, Griffiths, Dayna, Hodgkinson, Suzanne, Lechner-Scott, Jeannette, Lee, Andrew, Malhotra, Ram, McCombe, Pamela, Parratt, John, Plummer, Christopher, Van der Walt, Anneke, Martel, Kate and Walker, Rob (2023). Novel real world evidence from MSGo, a digital support program for secondary progressive multiple sclerosis patients in Australia using Siponimod. PACTRIMS 2022: 12th Pan-Asian Committee for Treatment and Research in Multiple Sclerosis, Singapore, Singapore, 24-26 November 2022. London, United Kingdom: Sage Publications. |
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2023 Journal Article Early non-disabling relapses are important predictors of disability accumulation in people with relapsing-remitting multiple sclerosisDaruwalla, Cyrus, Shaygannejad, Vahid, Ozakbas, Serkan, Havrdova, Eva Kubala, Horakova, Dana, Alroughani, Raed, Boz, Cavit, Patti, Francesco, Onofrj, Marco, Lugaresi, Alessandra, Eichau, Sara, Girard, Marc, Prat, Alexandre, Duquette, Pierre, Yamout, Bassem, Khoury, Samia J., Sajedi, Seyed Aidin, Turkoglu, Recai, Altintas, Ayse, Skibina, Olga, Buzzard, Katherine, Grammond, Pierre, Karabudak, Rana, van der Walt, Anneke, Butzkueven, Helmut, Maimone, Davide, Lechner-Scott, Jeannette, Soysal, Aysun, John, Nevin ... Brown, J William L (2023). Early non-disabling relapses are important predictors of disability accumulation in people with relapsing-remitting multiple sclerosis. Multiple Sclerosis, 29 (7), 875-883. doi: 10.1177/13524585231151951 |
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2023 Journal Article Comparative effectiveness of autologous hematopoietic stem cell transplant vs fingolimod, natalizumab, and ocrelizumab in highly active relapsing-remitting multiple sclerosisKalincik, Tomas, Sharmin, Sifat, Roos, Izanne, Freedman, Mark S., Atkins, Harold, Burman, Joachim, Massey, Jennifer, Sutton, Ian, Withers, Barbara, Macdonell, Richard, Grigg, Andrew, Torkildsen, Øivind, Bo, Lars, Lehmann, Anne Kristine, Havrdova, Eva Kubala, Krasulova, Eva, Trněný, Marek, Kozak, Tomas, van der Walt, Anneke, Butzkueven, Helmut, McCombe, Pamela, Skibina, Olga, Lechner-Scott, Jeannette, Willekens, Barbara, Cartechini, Elisabetta, Ozakbas, Serkan, Alroughani, Raed, Kuhle, Jens, Patti, Francesco ... MSBase Study Group Authors (2023). Comparative effectiveness of autologous hematopoietic stem cell transplant vs fingolimod, natalizumab, and ocrelizumab in highly active relapsing-remitting multiple sclerosis. JAMA Neurology, 80 (7), 702-713. doi: 10.1001/jamaneurol.2023.1184 |
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2023 Journal Article Variability of the response to immunotherapy among subgroups of patients with multiple sclerosisDiouf, Ibrahima, Malpas, Charles B., Sharmin, Sifat, Roos, Izanne, Horakova, Dana, Havrdova, Eva Kubala, Patti, Francesco, Shaygannejad, Vahid, Ozakbas, Serkan, Izquierdo, Guillermo, Eichau, Sara, Onofrj, Marco, Lugaresi, Alessandra, Alroughani, Raed, Prat, Alexandre, Girard, Marc, Duquette, Pierre, Terzi, Murat, Boz, Cavit, Grand'Maison, Francois, Hamdy, Sherif, Sola, Patrizia, Ferraro, Diana, Grammond, Pierre, Turkoglu, Recai, Buzzard, Katherine, Skibina, Olga, Yamout, Bassem, Altintas, Ayse ... Kalincik, Tomas (2023). Variability of the response to immunotherapy among subgroups of patients with multiple sclerosis. European Journal of Neurology, 30 (4), 1014-1024. doi: 10.1111/ene.15706 |
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2023 Journal Article Sensitivity and specificity of the ECAS in identifying executive function and social cognition deficits in MNDTjokrowijoto, Priscilla, Phillips, Mia, Ceslis, Amelia, Henderson, Robert D., McCombe, Pamela A. and Robinson, Gail A. (2023). Sensitivity and specificity of the ECAS in identifying executive function and social cognition deficits in MND. Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration, 24 (5-6), 466-474. doi: 10.1080/21678421.2023.2188053 |
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2023 Journal Article Comparative effectiveness in multiple sclerosis: a methodological comparisonRoos, Izanne, Diouf, Ibrahima, Sharmin, Sifat, Horakova, Dana, Havrdova, Eva Kubala, Patti, Francesco, Shaygannejad, Vahid, Ozakbas, Serkan, Izquierdo, Guillermo, Eichau, Sara, Onofrj, Marco, Lugaresi, Alessandra, Alroughani, Raed, Prat, Alexandre, Girard, Marc, Duquette, Pierre, Terzi, Murat, Boz, Cavit, Grand’Maison, Francois, Sola, Patrizia, Ferraro, Diana, Grammond, Pierre, Turkoglu, Recai, Buzzard, Katherine, Skibina, Olga, Yamou, Bassem, Altintas, Ayse, Gerlach, Oliver, van Pesch, Vincent ... Kalincik, Tomas (2023). Comparative effectiveness in multiple sclerosis: a methodological comparison. Multiple Sclerosis Journal, 29 (3), 326-332. doi: 10.1177/13524585231151394 |
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2023 Journal Article Case report: Adult-onset limb girdle muscular dystrophy in sibling pair due to novel homozygous LAMA2 missense variantKatz, Matthew, Waddell, Leigh B., Yuen, Michaela, Bryen, Samantha J., Oates, Emily, Garton, Fleur C., Robertson, Thomas, Henderson, Robert David, Cooper, Sandra T. and McCombe, Pamela A. (2023). Case report: Adult-onset limb girdle muscular dystrophy in sibling pair due to novel homozygous LAMA2 missense variant. Frontiers in Neurology, 14 1055639, 1055639. doi: 10.3389/fneur.2023.1055639 |
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2023 Journal Article Muscle and its neuromuscular synapse – players in the pathogenesis of motor neuron diseaseNoakes, Peter G., Phillips, William D., Jeffree, Rosalind L., Steyn, Frederik J., Wolvetang, Ernst J., Henderson, Rob D., McCombe, Pamela A. and Ngo, Shyuan T. (2023). Muscle and its neuromuscular synapse – players in the pathogenesis of motor neuron disease. Journal of Experimental Neurology, 4 (1), 1-5. doi: 10.33696/neurol.4.067 |
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2023 Journal Article Phenotypic variability within the desminopathies: A case series of three patientsYeow, Dennis, Katz, Matthew, Henderson, Robert, Prasad, Sandhir, Denman, Russell, Blum, Stefan, Davis, Mark, Robertson, Thomas and McCombe, Pamela (2023). Phenotypic variability within the desminopathies: A case series of three patients. Frontiers in Neurology, 13 1110934. doi: 10.3389/fneur.2022.1110934 |
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2023 Other Outputs Skeletal muscle and blood RNA-seq counts in motor neurone disease cases and controlsAnna Freydenzon, Allan F. McRaee, Shyuan Ngo, Naomi R. Wray, Leanne Wallace, Anjali K. Henders, Pamela A. McCombe, Robert D. Henderson and Frederik J. Steyn (2023). Skeletal muscle and blood RNA-seq counts in motor neurone disease cases and controls. The University of Queensland. (Dataset) doi: 10.48610/b722f1f |
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2023 Journal Article Heterogeneity on long-term disability trajectories in patients with secondary progressive MS: a latent class analysis from Big MS Data networkSignori, Alessio, Lorscheider, Johannes, Vukusic, Sandra, Trojano, Maria, Iaffaldano, Pietro, Hillert, Jan, Hyde, Robert, Pellegrini, Fabio, Magyari, Melinda, Koch-Henriksen, Nils, Sørensen, Per Soelberg, Spelman, Tim, van der Walt, Anneke, Horakova, Dana, Havrdova, Eva, Girard, Marc, Eichau, Sara, Grand'Maison, Francois, Gerlach, Oliver, Terzi, Murat, Ozakbas, Serkan, Skibina, Olga, Van Pesch, Vincent, Sa, Maria Jose, Prevost, Julie, Alroughani, Raed, McCombe, Pamela A, Gouider, Riadh, Mrabet, Saloua ... Butzkueven, Helmut (2023). Heterogeneity on long-term disability trajectories in patients with secondary progressive MS: a latent class analysis from Big MS Data network. Journal of Neurology, Neurosurgery and Psychiatry, 94 (1), 23-30. doi: 10.1136/jnnp-2022-329987 |
